Breakthrough 科学

We relentlessly pursue bold science to translate genetic discoveries into new medicines that advance the future of human health.

了解更多

Focus on Patients

We listen to and learn from patient communities to collaborate on solutions with the potential to help improve care.

了解更多

People-First Culture

Our talented and dedicated people represent the best the biotech industry has to offer and have helped shape a culture focused on working together to deliver for the patients we serve.

了解更多

博彩平台网址大全 is a global biotechnology company with eight marketed products that treat life-threatening conditions.

Since our founding in 1997, we’ve applied our scientific expertise in understanding the underlying causes of genetic conditions to create transformative medicines, using a number of treatment modalities. Our approved medicines treat achondroplasia, severe hemophilia A and several rare inherited and lysosomal storage diseases. We’re also advancing an industry-leading pipeline of investigational medicines that are in various stages of clinical and preclinical development.

了解更多

加入博彩平台网址大全的团队

Come work with us. 搜索 our global career opportunities to learn how you can make your mark.

Explore Opportunities